Apazunersen is an antisense oligonucleotide (ASO) that targets and inhibits expression of the UBE3A antisense transcript (UBE3A-AS) to prevent silencing of the paternally inherited allele of the UBE3A gene and reactivate expression of the deficient protei
分子式
C184H224N67O96P17S17
分子量
5981.79
CAS号
2919324-01-7
运输条件
Room temperature in continental US; may vary elsewhere.