Basivarsen (DYNE-101 oligomer) is composed of an antisense oligonucleotides and a linker . It is designed to target mutant nuclear myotonic dystrophy protein kinase (DMPK) RNA for RHase H-mediated degradation to correct splicing. It is used for the study of myotonic dystrophy type 1 (DM1).
分子量
6726.91
CAS号
3028750-61-7
运输条件
Room temperature in continental US; may vary elsewhere.